Patients Updates

Pompe Disease

Clinical Research Study:  VAL-1221 Delivered Intravenously in Ambulatory and Ventilator-free Patients With Late-Onset Pompe Disease.  For more information on the study please see www.clinicaltrials.gov entry (https://clinicaltrials.gov/ct2/show/NCT02898753?term=val-1221&rank=1)